SITC Release Criteria Virtual Summit Executive Summary

In the summer of 2022, SITC convened cellular therapy experts from academia, government, and industry to identify significant regulatory hurdles facing cellular therapies as they relate to the Investigational New Drug Application (IND) and Biological License Application (BLA) regulatory review. These hurdles and potential solutions were detailed within an initial Cellular Therapy Regulatory Summit EXECUTIVE SUMMARY. While many hurdles were identified, the topic concerning potency assays and release criteria specifications was selected as the most critical hurdle. In order to address this, SITC reconvened experts in 2023 to focus specifically on release criteria and the role of potency. 

Summit attendees were divided into three expert panels each addressing a significant hurdle identified by the summit organizers:

  • Panel 1: Release criteria for current commercial products 

  • Panel 2: Potency as a release criterion

  • Panel 3: Future development of ideal release criteria 

These panels worked to identify key hurdles and propose potential solutions across these topics. The results from the summit can be found within the Release Criteria EXECUTIVE SUMMARY. 

Outcomes & Next Steps

Summit attendees formalized possible solutions towards addressing the hurdles associated with release criteria throughout the program. At the conclusion of the meeting, SITC was provided with five key efforts that would create momentum in this arena:


COMMENT

Commentary papers and meetings on future/past FDA guidance documents related to release criteria specifications

  • SITC has provided comment on the recently released FDA guidance on potency in January of 2024. The comments provided reflected the outcomes and discussions held at the summit

CONVENE

Future consensus meetings to address the hurdles specifically stated within the summit report


PUBLISH

Development of future manuscripts:

  • Addressing and defining the relevance/necessity of potency assays and release criteria
  • Commenting on existing FDA guidance related to, cellular therapy development, potency assays and release criteria

AMPLIFY

Leverage the SITC annual meeting and other national scientific meetings to amplify these efforts for fieldwide adoption


COLLABORATE

Collaborate with other like-minded societies including:

  • Future collaborative meetings with FDA to share results from summit

Organizers

Chantale Bernatchez, PhD

Chantale Bernatchez, PhD
The Cell Therapy Manufacturing Center

Patrick Hanley, PhD

Patrick Hanley, PhD
Children's National Hospital

Michael Kalos, PhD

Michael Kalos, PhD
Next Pillar Consulting

Raj Puri, MD, PhD

Raj Puri, MD, PhD
Iovance

SITC Cellular Therapy Regulatory Summit Executive Summary

The number of cellular and gene therapy-based oncology treatments being developed by the field has grown exponentially over the past ten years. As a result of this rapid advancement, many hurdles exist in the field that are causing delays in development and regulatory review of these important products. To help address this, the Society for Immunotherapy of Cancer (SITC) convened a Cellular Therapy Strategic Taskforce in 2021. The purpose of this taskforce was to formulate a strategic plan for the society aimed at increasing SITC’s overall impact in advancing the most promising cellular therapies to improve oncology patient care.

The strategic plan consisted of three key pillars including groundbreaking science, balanced educational content, and regulatory consensus. As a first step in facilitating regulatory consensus, SITC hosted the Cellular Therapy Regulatory Summit. This summit consisted of cellular therapy experts from academia, industry, and government meeting hybridly to further the goals of the SITC cellular therapy strategic plan.

Summit Goals and Structure

The main goal of the SITC Cellular Therapy Regulatory Summit was to identity the most significant hurdles facing cellular 
therapy researchers throughout the Investigational New Drug (IND) Application process. In order to facilitate this process, the 
attendees participated in a pre-summit survey asking them to assign a ranking of 1-5 for each hurdle, 5 meaning the hurdle is 
most important to address and 1 being of least importance. The identified hurdles included: 

  1. Potency Assays
  2. Which product attributes should be monitored and are indicative of potential changes in safety and efficacy?
  3. What is a ‘new product’ versus an iterative manufacturing upgrade (parent-child IND)
  4. Uniform Risk Evaluation and Mitigation Strategies (REMS) for future approvals
  5. Recommended number of copies per cell of vector
  6. Timing for measurement of a cell dose (eg, pre- or post-freeze)
  7. Replication competent lentivirus therapy and applications 

COMMENT

Commentary papers and meetings on future/past FDA guidance documents related to cellular therapies


CONVENE

Future consensus meetings to address the hurdles specifically stated within this report


PUBLISH

Development of future manuscripts addressing:

  • Defining the relevance/necessity of potency assays
  • Guidance on new product comparability
  • Commentary/review on existing FDA parent-child guidance
  • Revisions to REMS guidance and requirements

AMPLIFY

Leverage the SITC annual meeting and other national scientific meetings to amplify these efforts for field wide adoption


COLLABORATE

Collaborate with other like-minded societies including:

  • Friends of Cancer Research
  • Foundation for the Accreditation of Cellular Therapy
  • American Society for Transplantation and Cellular Therapies
  • International Society for Cell and Gene Therapy 

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